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'Bubble Boy' Cured by Gene Therapy in UK

DrKyle writes "Another child with "Bubble Boy" disease aka ADA-SCID (adenosine deaminase deficiency causing severe combined immunodeficiency) has been cured by transforming bone marrow stem cells with the functioning gene. Normally toxic levels of adenosine build up in T-cells killing off those important cells required for a robust immune system. While not the first person cured, another successful case of gene therapy goes a long way in encouraging goverments to continue to fund genetic research."

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  1. Other trials were shut down by rakarnik · · Score: 0, Redundant

    Three other trials using genetherapy to cure the same disease were shut down by the FDA just last week. http://www.cbsnews.com/stories/2005/03/04/tech/mai n678164.shtml Apparently, the "harmless virus" used in a French trial ended up causing cancer in two patients. TFA does not seem to mention these other trials.